Description and Appraisal of Outcome Measures - Clinical Review Report:  Eculizumab (Soliris) - NCBI Bookshelf

Description and Appraisal of Outcome Measures - Clinical Review Report: Eculizumab (Soliris) - NCBI Bookshelf

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To describe the following outcome measures and review their measurement properties (validity, reliability, responsiveness to change, and MID): Myasthenia Gravis Activities of Daily Living scale (MG-ADL)Quantitative Myasthenia Gravis (QMG) scoreMyasthenia Gravis Composite (MGC) scoreMyasthenia Gravis Quality of Life 15-item scale (MG-QoL15)Myasthenia Gravis Foundation of America Post-Intervention Status (MGFA-PIS)Quality of Life in Neurological Disorders Fatigue Scale (Neuro-QoL Fatigue)European Quality of Life (EuroQol) Health 5-Dimensions (EQ-5D) questionnaire.

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Full article: Quantifying the economic effects of ravulizumab

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Clinical Evidence - Clinical Review Report: Eculizumab (Soliris

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Clinical Evidence - Clinical Review Report: Eculizumab (Soliris

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Hematopoietic stem cell transplantation-associated thrombotic

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Costs and Utilization of New-to-Market Neurologic Medications

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Clinical Evidence - Clinical Review Report: Eculizumab (Soliris

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Clinically important change for the FACIT-Fatigue scale in

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The treatment of atypical hemolytic uremic syndrome with

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Clinical Evidence - Clinical Review Report: Eculizumab (Soliris

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Description and Appraisal of Outcome Measures - Clinical Review

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Eculizumab monotherapy for NMOSD: Data from PREVENT and its open

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Brain Sciences, Free Full-Text

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Ravulizumab: A Review in Atypical Haemolytic Uraemic Syndrome

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Economic Review - Pharmacoeconomic Report: Eculizumab (Soliris